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2024
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Invention
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Cpg reduced factor viii variants, compositions and methods and uses for treatment of hemostasis d... |
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Invention
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Lipid compounds. The present invention relates to lipids that include novel triazole, and alkyl- ... |
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Invention
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Inhibitory nucleic acid targeting alpha synuclein expression. The present invention features poly... |
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P/S
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Medical and scientific research, namely, conducting clinical trials for others in the field of Hu... |
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Invention
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Codon-optimized acid alpha-glucosidase expression cassettes and methods of using same.
The inven... |
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Invention
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Factor viii (fviii) gene therapy methods.
Methods of using vectors comprising nucleic acid and n... |
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Invention
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Inhibitory rna targeting huntingtin expression. The present invention features RNA polynucleotide... |
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P/S
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Scientific and medical research in the field of gene therapy; Research and development in the fie... |
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Invention
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Ppt1 gene therapy. The present invention features PPT1 polypeptides and encoding nucleic acid con... |
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2023
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Invention
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Adeno-associated virus formulations. Compositions and methods for the formulation and use of reco... |
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Invention
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Methods of regulating adeno-associated virus production.
The presently disclosed subject matter ... |
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P/S
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Providing medical and scientific research information in the field of clinical trials relating to... |
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P/S
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Providing medical and scientific research information in the
field of clinical trials relating t... |
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Invention
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Gene editing for controlled expression of episomal genes. Disclosed herein are methods for regula... |
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Invention
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Apoe gene therapy. The present relates to polynucleotide constructs encoding an ApoE3 related pro... |
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Invention
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Piperazine compounds. The present invention relates to novel piperazine compounds, in particular,... |
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Invention
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Enhancing non-viral dna delivery and expression. The present invention features method and compos... |
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Invention
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Immune enhancement and infectious disease treatment. The present invention features methods utili... |
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Invention
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Immune enhancement of cancer treatment. The present invention features methods utilizing nanopart... |
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P/S
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Ophthalmology services; optometry services; vision screenings; medical testing, namely, eye and v... |
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2022
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P/S
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Conducting employee incentive award programs to promote excellence in service in the field of gen... |
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Invention
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Adeno-associated virus-mediated crispr-cas9 treatment of ocular disease.
Disclosed herein are co... |
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Invention
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Method of enhancing gene therapy by targeting cgas-sting pathway.
The present invention features... |
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Invention
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Methods and composition for non-viral dna delivery. The present invention features method and com... |
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Invention
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Method of enhancing gene therapy by targeting cgas-sting pathway. The present invention features ... |
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Invention
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Aav vector column purification methods.
Described herein is methods for rAAV particles purificat... |
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Invention
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Methods of regulating adeno-associated virus production. The presently disclosed subject matter r... |
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Invention
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Aav vector column purification methods. Described herein is methods for rAAV particles purificati... |
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P/S
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Providing a website featuring medical and scientific research news on genetic testing and medical... |
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Invention
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Compositions and methods for treating hereditary angioedema.
Nucleic acids encoding C1 inhibitor... |
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Invention
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Compositions and methods for treating hereditary angioedema. Nucleic acids encoding Cl inhibitor ... |
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Invention
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Compositions and methods for treating fabry disease.
Polynucleotides including nucleic acids enc... |
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Invention
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Compositions and methods for treating fabry disease. Polynucleotides including nucleic acids enco... |
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2021
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Invention
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Methods of enhancing non-viral gene therapy.
Methods of delivering a transgene to a subject in n... |
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Invention
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Methods of enhancing non-viral gene therapy. Methods of delivering a transgene to a subject in ne... |
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P/S
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providing medical research information in the field of clinical trials in relation to hemophilia ... |
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P/S
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Patient health care coordination services for use in case management, namely, providing health ca... |
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Invention
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Compositions and methods for increasing or enhancing transduction of gene therapy vectors and for... |
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2020
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Invention
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Secretable protein induced immune tolerization and treatment of autoimmune, allergic and other di... |
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P/S
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Promoting public awareness of hemophilia, gene therapy research, genetic testing for medical purp... |
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Invention
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Aav vector treatment methods for late infantile neuronal ceroid lipofuscinosis type 2.
Disclosed... |
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Invention
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Aav vector treatment methods for late infantile neuronal ceroid lipofuscinosis type 2. Disclosed ... |
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2019
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Invention
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In vitro assay for detecting enhancers and inhibitors of adeno associated virus (aav) vector tran... |
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Invention
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Optimized promoter sequences, intron-free expression constructs and methods of use. The disclosur... |
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P/S
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Educational materials in electronic form, namely, downloadable slides, letters, and brochures per... |
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Invention
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Codon-optimized acid alpha-glucosidase expression cassettes and methods of using same. The invent... |
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Invention
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Plasmid free aav vector producing cell lines.
Disclosed herein are packaging cell lines, in whic... |
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P/S
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Providing health information online in the field of Pompe disease and gene therapy for Pompe dise... |
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Invention
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Engineered aav capsids with increased tropism and aav vectors comprising the engineered capsids a... |
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P/S
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providing medical research information in the field of clinical trials in relation to hemophilia;... |
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2018
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Invention
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Adeno-associated virus (aav) vector lipid nanoparticle compositions and methods of use.
A compos... |
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P/S
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Providing a website featuring news and information about the causes of inherited retinal disease ... |
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P/S
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Health information services, namely, providing information related to the treatment of retinal di... |
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Invention
|
Aav vector column purification methods.
Described and provided herein are purification, producti... |
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P/S
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Providing information for patients, families and health care providers about health care insuranc... |
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2017
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P/S
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Providing education in the field of potential genetic therapy
Providing a website featuring educa... |
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P/S
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Promoting public awareness of inherited retinal diseases (IRD), gene therapy research, and geneti... |
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P/S
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Arranging advisory boards that offer business management consulting services in the field of heal... |
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Invention
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Relative potency assay for viral vector encoding isomerohydrolases.
Methods for assaying functio... |
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P/S
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Biologic preparations for the treatment of retinal diseases |
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P/S
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Biologic preparations for the treatment of retinal diseases. |
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Invention
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Column-based fully scalable raav manufacturing process. In accordance with the invention, provide... |
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P/S
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Biologic preparations for use in the treatment of genetically based diseases and disorders, namel... |
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P/S
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Biologic preparations for use in the treatment of genetically based diseases and disorders; Biolo... |
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P/S
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Genetic testing for medical purposes |
