|
2025
|
P/S
|
nucleotides for scientific and research use pharmaceutical preparations research and development ... |
|
|
Invention
|
Methods for treating conditions and diseases. VSCN1ASCN1A gene. The dosing regimens and methods c... |
|
|
Invention
|
Treatment of eye diseases and diagnostics. e.g.,OPA1e.g., e.g., low-contrast visual acuity test) ... |
|
|
Invention
|
Compounds for treatment of conditions and diseases.
Compounds are provided herein that can promo... |
|
2024
|
Invention
|
Methods for treating conditions and diseases.
Provided herein are methods for treating condition... |
|
|
Invention
|
Methods for treating conditions and diseases. SCN1ASCN1A gene and modulating the expression level... |
|
|
Invention
|
Opa1 antisense oligomers for treatment of conditions and diseases. Alternative splicing events in... |
|
|
Invention
|
Opa1 antisense oligomers for treatment of conditions and diseases.
Agents that target a processe... |
|
|
Invention
|
Compounds and methods for treating human subjects. Described herein are compounds and methods tha... |
|
|
Invention
|
Antisense oligomer formulations. VVV1.1 protein in the subject. |
|
2023
|
Invention
|
Antisense oligomers for treatment of non-sense mediated rna decay based conditions and diseases. ... |
|
|
Invention
|
Antisense oligomers for treatment of conditions and diseases.
Alternative splicing events in SCN... |
|
|
Invention
|
Opa1 antisense oligomers for treatment of conditions and diseases.
Alternative splicing events i... |
|
|
Invention
|
Compositions for treatment of conditions and diseases associated with polycystin expression.
Alt... |
|
|
Invention
|
Compounds for treatment of conditions and diseases. SCN1ASCN1ASCN1A gene and can modulate the exp... |
|
2022
|
Invention
|
Opa1 antisense oligomers for treatment of conditions and diseases. e.g.e.g.e.g., via modulation o... |
|
|
Invention
|
Compositions and methods for modulating splicing and protein expression.
Alternative splicing ev... |
|
|
Invention
|
Compositions for treatment of conditions and diseases associated with polycystin expression. Alte... |
|
2021
|
Invention
|
Methods and compositions for modulating splicing of alternative introns.
Provided herein are met... |
|
|
Invention
|
Methods and compositions for modulating splicing and translation.
Alternative splicing events in... |
|
|
Invention
|
Antisense oligomers and uses thereof.
Provided herein are methods and compositions for increasin... |
|
|
Invention
|
Antisense oligomers for treatment of autosomal dominant mental retardation-5 and dravet syndrome.... |
|
2020
|
Invention
|
Antisense oligomers for treatment of conditions and diseases. Alternative splicing events in SCN1... |
|
|
Invention
|
Antisense oligomers for treatment of conditions and diseases. SCN1ASCN1ASCN1A gene can modulate t... |
|
|
Invention
|
Compositions and methods for modulating splicing and protein expression. Alternative splicing eve... |
|
|
Invention
|
Methods and compositions for modulating splicing of alternative introns. Provided herein are meth... |
|
|
Invention
|
Methods and compositions for modulating splicing and translation. Alternative splicing events in ... |
|
2019
|
Invention
|
Methods and compositions for treatment of cholesteryl ester storage disease. Provided herein are ... |
|
2018
|
Invention
|
Antisense oligomers and uses thereof. Provided herein are methods and compositions for increasing... |
|
2016
|
Invention
|
Compositions and methods for treatment of liver diseases. Provided herein are methods and composi... |
|
|
Invention
|
Compositions and methods for treatment of kidney diseases. Provided herein are methods and compos... |
|
|
Invention
|
Antisense oligomers for treatment of alagille syndrome. Provided herein are methods and compositi... |
|
|
Invention
|
Antisense oligomers for treatment of polycystic kidney disease. Provided herein are methods and c... |
|
|
P/S
|
Pharmaceuticals and medical preparations. Scientific research and development; Research and devel... |
|
|
P/S
|
Pharmaceutical preparations for the treatment of inherited diseases and genetic diseases, namely ... |
|
|
P/S
|
Research and development in the field of bioscience |
