2023
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Invention
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Adeno-associated virus compositions for arsa gene transfer and methods of use thereof. Provided h... |
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Invention
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Liver de-targeted recombinant aav capsid proteins.
Provided herein are recombinant adeno-associa... |
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Invention
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Liver de-targeted recombinant aav capsid proteins. Provided herein are recombinant adeno-associat... |
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Invention
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Bidirectional dual promoter expression vectors and uses thereof.
Provided herein are polynucleot... |
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Invention
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Bidirectional dual promoter expression vectors and uses thereof. Provided herein are polynucleoti... |
2022
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Invention
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Methods and compositions for the production of adeno-associated virus.
Provided herein are metho... |
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Invention
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Methods and compositions for the production of adeno-associated virus. Provided herein are method... |
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Invention
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Methods and compositions for the purification of adeno-associated virus.
Provided herein are met... |
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Invention
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Methods and compositions for the purification of adeno-associated virus. Provided herein are meth... |
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Invention
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Non-naturally occurring polyadenylation elements and methods of use thereof.
Provided herein are... |
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Invention
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Non-naturally occurring polyadenylation elements and methods of use thereof. Provided herein are ... |
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Invention
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Adeno-associated virus formulations.
Provided herein are pharmaceutical compositions (e.g., form... |
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Invention
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Adeno-associated virus formulations. Provided herein are pharmaceutical compositions (e.g., formu... |
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Invention
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Adeno-associated virus packaging systems.
Provided herein is a dual vector transfection system f... |
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Invention
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Adeno-associated virus packaging systems. Provided herein is a dual vector transfection system fo... |
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Invention
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Adeno-associated virus compositions and methods of use thereof.
Provided herein are novel adeno-... |
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Invention
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Adeno-associated virus compositions and methods of use thereof. Provided herein, inter alia, are ... |
2021
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Invention
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Adeno-associated virus compositions for arsa gene transfer and methods of use thereof.
Provided ... |
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Invention
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Gene therapy methods.
Provided are methods for reducing the risk of occurrence and/or the severi... |
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Invention
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Improved gene therapy methods. Provided are methods for reducing the risk of occurrence and/or th... |
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Invention
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Improved gene therapy methods. e.g.S. pneumoniae S. pneumoniae infection) in a subject that is re... |
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Invention
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Vectorized antibodies and uses thereof.
Provided are recombinant adeno-associated virus (rAAV) c... |
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Invention
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Vectorized antibodies and uses thereof. e.g.e.g., Paroxysmal Nocturnal Hemoglobinuria)). Also pro... |
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G/S
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Pharmaceuticals, excluding pharmaceuticals for the treatment of genetic diseases and disorders. |
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Invention
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Adeno-associated virus compositions for restoring pah gene function and methods of use thereof. e... |
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Invention
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Adeno-associated virus compositions for ids gene transfer and methods of use thereof.
Provided a... |
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Invention
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Adeno-associated virus compositions for ids gene transfer and methods of use thereof. e.g.e.g., H... |
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G/S
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Pharmaceutical preparations and compositions for the treatment of human genetic diseases and diso... |
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G/S
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Pharmaceuticals for human use. |
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Invention
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Methods of treating phenylketonuria. Provided herein are methods of treating a subject having a d... |
2020
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Invention
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Adeno-associated virus compositions and methods of use thereof. Provided herein are novel adeno-a... |
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G/S
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House mark for pharmaceuticals |
2019
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G/S
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Pharmaceuticals. Pharmaceutical research and development services. |
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Invention
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Adeno-associated virus compositions for restoring f8 gene function and methods of use thereof. Pr... |
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Invention
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Adeno-associated virus compositions for restoring pah gene function and methods of use thereof.
... |
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Invention
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Adeno-associated virus compositions for pah gene transfer and methods of use thereof. Provided he... |
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Invention
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Adeno-associated virus compositions for restoring pah gene function and methods of use thereof. P... |
2018
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Invention
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Adeno-associated virus compositions for restoring hbb gene function and methods of use thereof. P... |
2017
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G/S
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Pharmaceutical preparations and compositions for the treatment of human genetic disorders; pharma... |
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G/S
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Pharmaceutical research and development services |
2016
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G/S
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Pharmaceuticals for the treatment of genetic diseases and disorders |